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MODULATION OF NUCLEAR-RETAINED RNA

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专利名称:MODULATION OF NUCLEAR-RETAINED RNA发明人:Bennett, C. Frank申请号:AU2016269447申请日:20161206

公开号:AU2016269447B2公开日:20181213

摘要:#$%^&*AU2016269447B220181213.pdf##### Abstract Provided herein aremethods, compounds and compositions for reducing expression of a nurclear-retainedRNA 'nrRNA' in an animal. Also provided herein are methods compounds and

compositions for treating, ameliorating, delaying or reducing a symptom of a disease ordisorder associated with a nrRNA in an animal.

申请人:Ionis Pharmaceuticals, Inc.

代理人:Pizzeys Patent and Trade Mark Attorneys Pty Ltd

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